The Latest Breaking News from Gene Therapy

An estimated 295 million people suffer from visual impairment globally. Around 43 million of those people are living with blindness. While not every form of blindness can be cured, recent scientific breakthroughs have uncovered new ways to treat some forms of inherited blindness through gene therapy.

Nicola Kelleher's partner Bradley Benjamin has a hereditary kidney disease which has seen him suffer on dialysis for years - and they didn't want the same outcome for their child

The FDA is considering greenlighting the experimental treatment under its accelerated approvals program. Some critics point out the therapy isn't yet proven to work and may be costly.

A world-first trial at UCL and UCLH has found a new gene therapy for Alzheimer's disease that is able to safely lower levels of the harmful tau protein known to cause the disease. Read further on Dynamite News:

Several FDA staffers were leaning toward rejecting a highly watched gene therapy from Sareptas, according to a report Thursday.

Gene therapies treat or prevent disease by tweaking the content or expression of cells' DNA.

In a surprise decision, the FDA will hold an advisory committee to discuss Sarepta's gene therapy, and SRPT stock tanked Friday.

A cure for a deadly spinal disorder will be given out on the NHS after pioneering gene therapy costing £1.8million was approved today for infants before symptoms begin

Scientists in Bristol have experimented with the therapy on mice and found it effectively rewound their hearts by the equivalent of 10 human years - soon they hope to use it on heart failure patients

Sarepta could snag an accelerated approval for its muscular dystrophy gene therapy, analysts suggested Wednesday as SRPT stock rocketed.

Teddi Shaw suffers from deadly metachromatic leukodystrophy and had her stem cells removed and the faulty genes replaced