The Latest Breaking News from Gene Therapy

Both of these growth stocks are positioned for long-term success.

Treatment may be offered to hundreds with severe form of disease, most often found in people of Mediterranean, Asian and Middle Eastern heritage

Given as an infusion into the ear, the treatment works by replacing the faulty DNA which causes a type of inherited deafness known as DFNB9.

Study participants born unable to hear could locate sound sources, recognise speech and dance to music after treatment

After the gene therapy, the children went from being profoundly deaf to having mild to moderate hearing loss

For countless families in India, rare diseases are a crippling burden. Affecting less than 1 in 50,000 individuals, these conditions often leave patients and doctors entangled in a frustrating diagnostic labyrinth. Traditional methods can lead to delays and misdiagnosis, further jeopardizing timely intervention. However, a beacon of hope emerges in…

The Lovatos relocated from Guatemala to Ohio for their son, who has the rare genetic disorder Canavan disease

Seven months after her treatment, the baby girl can now respond to her parents' voices without the aid of a cochlear implant.

Hospital to take unprecedented step after drug firm pulled out despite successful trial of treatment